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项与 ANB-004(Biocad) 相关的临床试验An Open-Label, Non-Comparative Clinical Study of the Safety and Efficacy of an Adeno-Associated Viral Vector Carrying the SMN Gene (ANB-004 (JSC BIOCAD, Russia)) After a Single Intravenous Administration of Escalating Doses in Children With Spinal Muscular Atrophy
The goal of this multicenter, open-label, non-comparative, cohort study is to investigate the safety, immunogenicity, and efficacy of ANB-004 in children with spinal muscular atrophy. The study will have a standard 3+3 dose-escalation design.
100 项与 ANB-004(Biocad) 相关的临床结果
100 项与 ANB-004(Biocad) 相关的转化医学
100 项与 ANB-004(Biocad) 相关的专利(医药)
100 项与 ANB-004(Biocad) 相关的药物交易