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非在研适应症- |
最高研发阶段临床1/2期 |
首次获批国家/地区- |
首次获批日期1800-01-20 |
An Open-label Phase I/II Study of JR-446 in Mucopolysaccharidosis Type IIIB
A Phase I/ II, open-label study, designed to evaluate the safety and explore efficacy of the study drug in development for the treatment of MPS IIIB patients.
100 项与 TfR1 x NAGLU 相关的临床结果
100 项与 TfR1 x NAGLU 相关的转化医学
0 项与 TfR1 x NAGLU 相关的专利(医药)