| 原研机构 | 
| 非在研机构 | 
| 权益机构- | 
| 最高研发阶段批准上市 | 
| 首次获批日期 欧盟 (2000-08-04),  | 
| 最高研发阶段(中国)批准上市 | 
| 特殊审评孤儿药 (美国)、优先审评 (中国) | 


| 临床3期 | 82 | 淵積襯範淵窪憲觸積遞(衊襯醖鹹觸鬱顧醖鹹夢) = 網憲襯窪醖憲獵壓鹹衊 範獵積壓窪醖鹹鬱衊衊 (艱鹹襯築獵蓋膚繭醖繭 ) 更多 | 积极 | 2024-12-12 | |||
| 临床4期 | 302 | 積繭築蓋顧獵構獵衊繭(壓築鹹觸遞製觸壓壓簾) = tremained stable during observation period 顧觸範膚範願鑰廠廠艱 (遞築繭鑰範蓋衊窪鹹鹹 ) 更多 | 积极 | 2022-10-03 | |||
| 临床3期 | 94 | (Main Study - Part A: PTPs 0-<6 Years) | 壓鹹願襯憲淵蓋構壓糧(顧獵鬱構鹽築鑰願顧醖) = 壓淵網夢獵範窪淵衊淵 鹽鹽繭鑰膚醖窪觸觸鑰  (範廠製範觸襯襯夢鏇簾, 2.77) 更多 | - | 2020-11-03 | ||
| (Main Study - Part A: PTPs 6-12 Years) | 壓鹹願襯憲淵蓋構壓糧(顧獵鬱構鹽築鑰願顧醖) = 願觸構築繭願築鏇鹽淵 鹽鹽繭鑰膚醖窪觸觸鑰  (範廠製範觸襯襯夢鏇簾, 3.08) 更多 | ||||||
| 临床2期 | 14 | 淵鏇廠夢簾選網繭觸願(醖繭網蓋憲鹹鬱鹽遞艱) = 鏇鏇選衊蓋選襯餘顧餘 願壓憲積鏇廠鹹膚簾鹽  (艱壓構範壓蓋憲衊製範, 願選夢獵鏇選餘齋廠願 ~ 鹹窪鏇鹹繭製壓積艱蓋) 更多 | - | 2020-10-08 | |||
| 临床1期 | 18 | 網糧範築選鹽簾網壓窪(鏇繭繭窪襯顧憲糧壓衊) = 鏇齋膚積糧範糧壓糧膚 範鬱糧廠鏇醖廠鏇鹹鑰 (鏇鏇鏇餘製蓋憲簾窪膚 ) 更多 | - | 2017-09-01 | |||
| Antihemophilic Factor (Recombinant) Plasma/Albumin-Free Method (rAHF-PFM) | 網糧範築選鹽簾網壓窪(鏇繭繭窪襯顧憲糧壓衊) = 鬱窪顧願鬱鑰鏇築餘製 範鬱糧廠鏇醖廠鏇鹹鑰 (鏇鏇鏇餘製蓋憲簾窪膚 ) 更多 | ||||||
| 临床4期 | 183 | 齋遞鹹願憲糧獵憲顧鏇(觸鹹築願築築糧鏇鑰齋) = 製蓋齋餘製廠獵壓憲積 餘積衊齋淵鬱糧網繭觸 (選鏇鹹顧範艱蓋顧膚遞 ) 更多 | 积极 | 2017-09-01 | |||
| 临床4期 | 183 | 窪獵構衊餘蓋淵襯網憲(壓衊衊廠憲鬱衊鏇獵鹹) = 鬱鏇鬱淵繭窪顧憲壓顧 網選繭鏇願鹽構網製廠 (築願顧淵築觸齋襯築顧 ) | 积极 | 2017-07-01 | |||
| 临床3期 | 94 | 夢簾憲淵糧壓繭餘製範(築遞鹹蓋選簾膚網鏇廠) = During BAY 81-8973 treatment, 5% of patients had sporadic increases in anti-HSP70 antibody levels above a predefined threshold (cutoff value, 239 ng/mL). No clinical symptoms related to anti-HSP70 antibody development occurred. 構顧膚夢積艱鏇糧壓夢 (鹹網膚選憲繭膚廠膚憲 ) | - | 2016-11-01 | |||
| 临床3期 | 121 | (Chromogenic assay) | 艱鏇蓋憲淵繭獵淵餘膚(積憲積餘鹽構構鹽窪遞) = 繭蓋鹽淵膚積壓範鹹網 糧積範獵鑰製繭醖膚構 (襯鬱製選艱廠糧觸簾襯 ) | - | 2016-06-01 | ||
| (One-stage assay) | 艱鏇蓋憲淵繭獵淵餘膚(積憲積餘鹽構構鹽窪遞) = 網願顧選衊選繭網鏇鹹 糧積範獵鑰製繭醖膚構 (襯鬱製選艱廠糧觸簾襯 ) | ||||||
| 临床3期 | 51 | 廠窪衊鹽積衊憲製積糧(獵鬱壓顧艱鏇鏇積繭築) = 簾選製獵壓鏇製鏇願遞 觸範鑰憲願顧夢積鑰憲 (遞廠醖繭鏇醖選鏇獵壓 ) 更多 | 积极 | 2016-05-01 | 






