The Children's Hospital of Philadelphia

iStock, Yulia Sutyagina The new policy, revealed by the Department of Health and Human Services on Wednesday, would make vaccines “less available and less affordable,” according to vaccine expert Paul Offit. It could also further complicate the picture for companies like Novavax. After a month that began with a missed PDUFA deadline for Novavax’s COVID-19 vaccine—and subsequent debate in both online and social media over FDA expectations for the company to complete another clinical trial—the picture might be becoming clearer. Or less so. Wednesday, the Department of Health and Human Services said it will require all new vaccines be tested in placebo-controlled trials before they are approved. “All new vaccines will undergo safety testing in placebo-controlled trials prior to licensure—a radical departure from past practices,” an HHS spokesperson told The Washington Post in response to an inquiry about HHS Secretary Robert F. Kennedy Jr.’s comments on the measles vaccine and general vaccine policy. HHS did not clarify which vaccines this new policy would apply to, according to the Post . The Post noted that while vaccines for new pathogens are already tested versus placebo, new vaccines for other diseases are instead tested against existing interventions. Indeed, the FDA has to this point allowed vaccine makers to use prior clinical efficacy data rather than conduct new trials when submitting annual boosters such as for flu and COVID-19 for regulatory approval. The HHS did indicate to the Post that the new requirement would not affect the flu vaccine, which the agency stated “has been tried and tested for more than 80 years.” In a note to investors Thursday morning, Leerink Partners wrote that the new policy “is negative news for vaccine manufacturers,” including Merck, BioNTech and Moderna. “HHS’s judgment appears questionable and risky, in our view,” the analysts continued, adding that “placebo-controlled trials are unnecessary and unethical for many populations,” and “the world will look to other countries’ health authorities as the gold standards for vaccine testing.” Novavax’s vaccine, Nuvaxovid, which won emergency use authorization in July 2022, has been tested in in four randomized placebo-controlled trials . It was widely expected to win full approval on April 1. However, The Wall Street Journal reported last week that the FDA was requesting the company complete an additional randomized clinical trial, which vaccine experts told the publication could cost tens of millions of dollars . Novavax has maintained that this would be a postmarketing commitment. However, in a rare regulatory communication on X regarding a pending decision, FDA Commissioner Marty Makary wrote: “To be clear, this is a new product that Novavax is trying to introduce to the market with a study of a different product from 2021. New products require new clinical studies.” Apparently responding to the WSJ piece, Makary added, “Under this administration, we are prioritizing the Gold Standard of Science—not what saves pharma companies ‘tens of millions of dollars.’” Based on this statement, it appears possible that Wednesday’s news could introduce more uncertainty for the Maryland-based company. Kennedy has a long history as an anti-vaccine advocate—though HHS said in a statement that the secretary “is not anti-vaccine—he is pro-safety, pro-transparency, and pro-accountability,” according to the WSJ . Makary, for his part, has been critical of COVID-19 vaccines and mandates, particularly for boosters. According to the Post , medical and public health experts expressed concern that this testing change could mean that COVID, and potentially other vaccines, will need to undergo “costly” and “unnecessary” studies that would limit vaccine production and access. “You are watching the gradual dissolution of the vaccine infrastructure in this country,” Paul Offit, director of the Vaccine Education Center at Children’s Hospital of Philadelphia, told the publication. “The goal is to make vaccines less available and less affordable.” On a parallel front, HHS and the National Institutes of Health announced the launch of a next-generation universal vaccine platform for pandemic-prone viruses. The initiative, which uses a beta-propiolactone (BPL)-inactivated, whole-virus platform, will fund “NIH’s in-house development of universal influenza and coronavirus vaccines,” according to a Thursday HHS release . “Generation Gold Standard is a paradigm shift,” NIH Director Jay Bhattacharya said in a statement. “It extends vaccine protection beyond strain-specific limits and prepares for flu viral threats—not just today’s, but tomorrow’s as well—using traditional vaccine technology brought into the 21st century.”

– ZEVASKYN fills a critical need for people living with RDEB, a debilitating dermatological condition with no cure – – Approval based on the pivotal Phase 3 VIITAL™ study, showing ZEVASKYN resulted in significant wound healing and pain reduction after a single treatment with a favorable safety profile – – ZEVASKYN to be available through Qualified Treatment Centers beginning in 3Q 2025 – – Abeona Assist™ patient services program offers personalized support for eligible patients and families throughout their treatment journey with ZEVASKYN – – Rare Pediatric Disease Priority Review Voucher (PRV) granted by FDA – – Abeona Therapeutics ® to host conference call today, Tuesday, April 29, 2025, at 8:00 a.m. ET – CLEVELAND, OH, USA I April 29, 2025 I Abeona Therapeutics Inc. (Nasdaq: ABEO) today announced the U.S. Food and Drug Administration (FDA) has approved ZEVASKYN™ (pronounced as ‘ZEE-vah-skin’) (prademagene zamikeracel) gene-modified cellular sheets, also known as pz-cel, as the first and only autologous cell-based gene therapy for the treatment of wounds in adult and pediatric patients with recessive dystrophic epidermolysis bullosa (RDEB), a serious and debilitating genetic skin disease. There is no cure for RDEB and ZEVASKYN is the only FDA-approved product to treat RDEB wounds with a single application. “Today’s approval of ZEVASKYN represents a pivotal moment in the treatment of RDEB, answering the call of people living with the clinical, economic, and human impact of this devastating disease,” said Vish Seshadri, Ph.D., M.B.A., Chief Executive Officer of Abeona. “We have heard from the RDEB community that there is a persistent unmet need to reliably address RDEB wounds, especially those that are chronic and prone to infection. Through a single surgical application, ZEVASKYN can now offer people with RDEB the opportunity for wound healing and pain reduction in even the most severe wounds, as evidenced by the results from our pivotal Phase 3 study.” First-of-its-kind gene therapy with robust body of clinical evidence The FDA approval of ZEVASKYN is based on the pivotal Phase 3 VIITAL™ study (NCT04227106), a multi-center, randomized, intrapatient-controlled trial that met its two co-primary efficacy endpoints demonstrating statistically significant healing of 50 percent or more from baseline in large chronic RDEB wounds, and pain reduction from baseline as assessed by the Wong-Baker FACES scale, as evaluated at six months after treatment. Across 43 large and chronic wounds treated with a single application of ZEVASKYN, 81 percent of wounds showed 50 percent or more healing (P<0.0001) as evaluated at six months, compared to 16 percent in 43 matched control wounds treated with standard of care. The most common adverse events were observed in fewer than five percent of patients and included procedural pain and itch. “ZEVASKYN was well-tolerated and efficacious in clinical studies, providing clinically meaningful improvements in wound healing, pain reduction, and other associated symptoms in large chronic RDEB wounds after a single application,” said Jean Tang, M.D., Ph.D., professor of dermatology and lead principal investigator of the VIITAL™ study. “In the completed Phase 1/2a study of ZEVASKYN, we have observed wound healing and pain reduction that have lasted for years after a single application. Today we can celebrate the availability of an exciting new therapeutic option made possible by the incredible courage of patients and families who participated in these clinical studies.” In the Phase 1/2a study of ZEVASKYN (NCT01263379), a single center, open label study in 38 chronic wounds across 7 patients showed that a single surgical application of ZEVASKYN was associated with long-term improvement at treated sites over a median follow-up of 6.9 years; range 4 to 8 years. “After many years of work, it is great to see this FDA approval of ZEVASKYN. The EB patients deserve all that we can do for them,” said M. Peter Marinkovich, M.D., associate professor of dermatology and co-principal investigator of the VIITAL™ study. “Based on the strength of our data across clinical trials, we are confident in ZEVASKYN’s ability to deliver long-term results after a single treatment application,” said Madhav Vasanthavada, Ph.D., M.B.A., Chief Commercial Officer of Abeona. “We are committed to working closely with both commercial and government payers on outcome-based agreements that stand behind the promise of ZEVASKYN for patients, and expedite access.” Across both clinical studies, ZEVASKYN was well-tolerated with no treatment-related serious adverse events observed to date. Anna L. Bruckner, MD, Co-Director of the EB Clinic at Children’s Hospital of Colorado and Professor of Dermatology, University of Colorado School of Medicine, said, “The FDA approval of ZEVASKYN marks a monumental step forward for individuals living with RDEB and their families, offering a much-needed, long-lasting treatment option for this devastating condition and providing hope for improved quality of life for these patients.” Amy Paller, M.D., pediatric dermatologist and clinical researcher, said, “Grafting gene-corrected skin onto chronically open wounds of patients with recessive dystrophic epidermolysis bullosa promises the potential to provide long-term healing of wounds, reduction in pain and reduced risk of infection. This therapeutic option will nicely complement recently approved topical products.” Dr. Seshadri added, “We are grateful to the patients, their families, and caregivers for their support of ZEVASKYN. We express our gratitude to debra of America for their unwavering support throughout the development journey, in particular, for their interactions with the FDA in support of ZEVASKYN and on behalf of the EB community that have helped make today’s regulatory approval possible. We are also thankful for the clinical study investigators, study site personnel, and the entire Abeona team for their collective commitment and determination through the development process, and contribution to this milestone achievement. We look forward to providing the RDEB community access to now-approved ZEVASKYN.” Addressing the underlying cause of RDEB With mutations in both copies of the COL7A1 gene that expresses Type VII collagen, people with RDEB have extremely fragile skin characterized by extensive blistering and severe wounds that often cover more than 30 percent of a patient’s body surface, and in some cases up to 80 percent. RDEB wounds cause debilitating pain and systemic complications impacting the length and quality of life. These wounds are difficult to heal, can remain open for years, and many that do close tend to reopen. ZEVASKYN consists of a patient’s own skin cells (keratinocytes) that have been genetically modified, to produce functional Type VII collagen. ZEVASKYN sheets are surgically applied to the patient’s wounded areas. In a single application of ZEVASKYN, up to 12 credit card-sized sheets can be joined together to cover large areas or applied to multiple distinct wounds, allowing for signficant coverage of affected body areas. Brett Kopelan, M.A., Executive Director of debra of America, the only national advocacy organization that provides all-inclusive care to the epidermolysis bullosa community, and father to Rafi, a teenager with RDEB, said, “I, and the team at debra of America, are very excited about the FDA’s approval of ZEVASKYN. Given that this therapeutic product addresses even the largest, most difficult, and problematic chronic wounds, we believe that the application of ZEVASKYN can significantly increase the quality of life of patients. Furthermore, I believe ZEVASKYN has the potential to transform the day-to-day standard of care for patients who suffer with these large chronic nonhealing wounds that cause significant pain and stress not only for the patient, but also for their caregivers. We are honored to have formed such a close relationship with Abeona over the years and look forward to deepening our partnership by helping ensure there is broad access for the patient population to ZEVASKYN, which I know is their ultimate goal.” Michael Hund, M.B.A., Chief Executive Officer of EB Research Partnership (EBRP), the largest global organization dedicated to funding research to treat and cure epidermolysis bullosa (EB), said, “The mission of EBRP is to advance commercially sustainable research aimed at treating and ultimately curing EB. We are honored to partner with the entire Abeona team and commend their leadership, determination, and passion to deliver much needed innovative solutions for individuals and their families living with EB. They continue to share our values and commitment to accelerate treatments to the EB community as quickly as possible. Abeona’s development and advancement of ZEVASKYN delivers a landmark moment for the global EB community, and their leadership in gene therapy holds so much promise to innovate the therapeutic landscape for not only EB, but many other rare diseases and conditions. EBRP is looking forward to collaborating with Abeona to continue to support the EB community.” ZEVASKYN availability in the third quarter of 2025 ZEVASKYN is expected to be available beginning in the third quarter of 2025 through ZEVASKYN Qualified Treatment Centers (QTCs). The QTCs are well-recognized epidermolysis bullosa treatment centers with cell and gene therapy experience, situated across the U.S. to ensure patients nationwide have access to this important treatment. Abeona’s comprehensive patient support program, Abeona Assist™, offers personalized support, including helping patients understand their insurance benefits and financial assistance options, and providing travel and logistical assistance for eligible patients. For more information on how to access ZEVASKYN, patients, caregivers, and providers may call Abeona Assist at 1-855-ABEONA-1 (1-855-223-6621) or email MyNavigator@AbeonaAssist.com . “We are grateful to the dedicated scientists whose work over the past decade made the development of ZEVASKYN possible,” said Marissa Perman, MD, Section Chief of Dermatology and Director of the Epidermolysis Bullosa Multidisciplinary Clinic at Children’s Hospital of Philadelphia and paid consultant to Abeona . “Having a new, uniquely differentiated, gene therapy for our patients with RDEB is a significant milestone in helping these special patients live fuller, pain-free and itch-free lives with less wounds. As a physician caring for patients with RDEB, I look forward to the opportunity to see this treatment in our practice.” Joyce Teng, MD, PhD, professor in dermatology with multiple hospital affiliations, said, “I’m thrilled to celebrate a groundbreaking advancement in therapeutic development for recessive dystrophic EB, a condition that has long needed an innovative solution. ZEVASKYN offers additional hope for patients and families affected by this painful and devastating skin disorder. This milestone is a testament to the dedication of scientists, researchers and medical professionals who have worked tirelessly to bring cutting edge treatments to those in need. It represents a scientific triumph, a profound step toward improving quality of life for individuals affected. We look forward to seeing the impact that this therapy will have on so many lives.” In connection with the FDA approval, Abeona received a Rare Pediatric Disease Priority Review Voucher (PRV). The Company plans to monetize the PRV. Conference Call Details Abeona Therapeutics will host a conference call and webcast with accompanying slides and patient videos today, Tuesday, April 29, 2025, at 8:00 a.m. ET. To access the call, dial 888-506-0062 (U.S. toll-free) or 973-528-0011 (international) and Entry Code: 320280 five minutes prior to the start of the call. A live, listen-only webcast and archived replay of the call can be accessed at https://investors.abeonatherapeutics.com/events . The archived webcast replay will be available for 30 days following the call. Indication ZEVASKYN TM (prademagene zamikeracel) is an autologous cell sheet-based gene therapy indicated for the treatment of wounds in adult and pediatric patients with recessive dystrophic epidermolysis bullosa (RDEB). Important Safety Information This is not a complete list of side effects. Patients should call their care team for medical advice about side effects. Side effects may be reported to Abeona at 1-844-888-2236 or FDA at 1-800-FDA-1088 or www.fda.gov/medwatch . See full Prescribing Information starting today, Tuesday, April 29, 2025, at approximately 7:00 a.m. ET. About Recessive Dystrophic Epidermolysis Bullosa Recessive dystrophic epidermolysis bullosa (RDEB), a rare connective tissue disorder without a cure, is characterized by severe skin wounds that cause pain and can lead to systemic complications impacting the length and quality of life. People with RDEB have a defect in both copies of the COL7A1 gene, leaving them unable to produce functioning type VII collagen, which is necessary to anchor the dermal and epidermal layers of the skin. About ZEVASKYN™ (prademagene zamikeracel) gene-modified cellular sheets or pz-cel ZEVASKYN is the first and only autologous cell sheet-based gene therapy for the treatment of wounds in adult and pediatric patients with recessive dystrophic epidermolysis bullosa (RDEB). RDEB is a severe skin disease caused by a defect in both copies of the COL7A1 gene resulting in the inability to produce functional type VII collagen. Without functional type VII collagen and anchoring fibrils, the skin is fragile and blisters easily, leading to wounds that continually open and close, or fail to heal altogether. Patients often have large open wounds that are at a high risk of systemic infection. ZEVASKYN incorporates the functional type VII collagen-producing COL7A1 gene into a patient’s own skin cells, ex vivo, using a replication-incompetent retroviral vector to produce functional type VII collagen in treated wounds. ZEVASKYN has demonstrated clinically meaningful wound healing and pain reduction with a single surgical application. For more information, visit www.ZEVASKYN.com . About Abeona Therapeutics Abeona Therapeutics Inc. is a commercial-stage biopharmaceutical company developing cell and gene therapies for serious diseases. Abeona’s ZEVASKYN™ (prademagene zamikeracel) is the first and only autologous cell-based gene therapy for the treatment of wounds in adults and pediatric patients with recessive dystrophic epidermolysis bullosa (RDEB). The Company’s fully integrated cell and gene therapy cGMP manufacturing facility in Cleveland, Ohio serves as the manufacturing site for ZEVASKYN commercial production. The Company’s development portfolio features adeno-associated virus (AAV)-based gene therapies for ophthalmic diseases with high unmet medical need. Abeona’s novel, next-generation AAV capsids are being evaluated to improve tropism profiles for a variety of devastating diseases. For more information, visit www.abeonatherapeutics.com . SOURCE: Abeona Therapeutics

Marks the First-Ever Global Pediatric Trial for Menin Inhibitors The PedAL (Pediatric Acute Leukemia) Master Trial is at the heart of LLS's Dare to Dream Project to transform treatment and care for kids with blood cancer WASHINGTON, April 21, 2025 /PRNewswire/ -- The Leukemia & Lymphoma Society (LLS) announced today the first pediatric patient has received treatment in a new subtrial of its Pediatric Acute Leukemia (PedAL) Master Clinical Trial (NCT04726241). PedAL is a first-of-its-kind integrated worldwide master trial that tests multiple targeted drugs simultaneously to accelerate treatments for leukemia, the most common childhood cancer. Infants and children with specific types of relapsed/refractory leukemia (KMT2A-rearranged, NUP98-rearranged, or NPM1-mutant acute leukemia) are now eligible to enroll in the subtrial, which is investigating a combination of chemotherapy and a menin inhibitor. This subtrial involves pediatric patients with some of the most common and hardest-to-treat leukemias. In fact, 80% of infants with acute lymphoblastic leukemia have a genetic rearrangement of the KMT2A gene. About 40% of infants with acute myeloid leukemia have one of the three specific types of leukemia that the trial's treatment targets1. Menin inhibitors are a new and promising class of drugs that block the interaction between other proteins and the menin protein. Research has shown that the menin protein is responsible for driving progression of certain types of leukemia. The new subtrial is open in North America at Children's Hospital of Philadelphia, Cincinnati Children's Hospital, St. Jude Children's Research Hospital, Memorial Sloan Kettering Cancer Center, Lurie Children's Hospital of Chicago and SickKids - The Hospital for Sick Children in Toronto. Global trial sites are open in Spain, the Netherlands, France and Austria. "It is rare for a trial to be so ambitious and forward thinking about the needs of children while studies in adults are still ongoing. The new subtrial is evaluating the safety, efficacy and dosing for the treatment of certain acute leukemias in pediatric patients," says E. Anders Kolb, M.D. President and Chief Executive Officer of The Leukemia & Lymphoma Society. "Historically, cancer treatments have been evaluated in adults first and if successful, then children. This has resulted in a nearly decade-long delay between when therapies are first available for adults compared to children." The new subtrial brings LLS one step closer to achieving its bold goal: By 2040, LLS will enable patients with blood cancer to gain more than one million years of life. New trial expands on PedAL, builds on success of LLS's Dare to Dream Project PedAL launched in 2022 with one treatment subtrial investigating venetoclax. That trial is now open at approximately 80 clinical sites in 19 countries across the globe. Enrollment in the treatment trials begins with the robust PedAL screening trial (NCT04726241), open in 179 sites in the United States, Canada, Australia and New Zealand. To date, the screening trial has enrolled almost 450 children to identify their unique tumor biology and help match them to any targeted treatment clinical trial they are eligible for, whether in or outside of PedAL. Because blood cancers are more common in adults, there is a larger incentive for new treatments to be developed in that population, and progress for pediatric acute leukemia has fallen behind. PedAL is changing this paradigm. A delay in research and the development of therapies for children with aggressive forms of cancer threatens their survival. Today, leukemia is the second leading cause of cancer deaths in children. And for children who survive, 80% develop life-altering and chronic health issues from their treatment. "More children are being diagnosed with leukemia today than ever before," says Kim Schuetz, an oncology nurse, an LLS Dare to Dream Ambassador and mother to Austin, who was diagnosed with acute lymphoblastic leukemia in 2011. "We need to study more treatment options for these children. Through Dare to Dream, we're striving to transform care, so they don't experience a laundry list of life-long health issues and the possibility of developing secondary cancers because of treatment from standard therapies, such as harmful chemotherapies." LLS has supported the development of menin inhibitors over two decades In the early 2000s, LLS provided funding to a group of bright scientific investigators, which led them to discover the menin protein inside cancer cells and its role in the devastating effects of certain forms of leukemia. Over the next several years, LLS provided more than $6 million through its venture philanthropy program, the Therapy Acceleration Program (TAP), to scientists at the University of Michigan. They discovered small molecule inhibitors of the interaction of two proteins, menin and KMT2A/MLL, that, when fused together, drive progression of AML. With TAP funding, the scientists demonstrated the activity of their compounds in the laboratory setting. To facilitate translation of the scientists' progress in the laboratory to the clinic, LLS introduced the scientists to a clinical-stage biopharmaceutical company. Helping children with blood cancer survive and thrive Dare to Dream is transforming treatment and care for kids with blood cancer, so they not only survive but thrive after treatment. PedAL is an integral part of LLS's Dare to Dream Project along with support services, advocacy efforts and funding for blood cancer research: Research: With 35 active academic research grants totaling more than $31 million in funding commitments to pediatric and adolescent and young adult research, LLS-funded investigators are conducting groundbreaking research including exploring the origins of pediatric blood cancers and investigating increased incidence and better treatment options for leukemia in children with Down Syndrome. Advocacy: To ensure that more kids with blood cancer have better access to care, LLS advocates for meaningful changes at the state and federal level. A recent victory was the reauthorization of the Childhood Cancer Survivorship, Treatment, Access and Research (STAR) Act, which expanded childhood cancer research and created plans to enhance the tracking and reporting of pediatric cancer cases and treatment outcomes. Education & Support Services: LLS continues to expand its free patient education and personalized support services for pediatric patients and families to provide guidance, information and comfort during treatment and beyond. "The successes of the Dare to Dream Project, now and in the future, positions us well to reach our bold goal of enabling blood cancer patients to gain more than one million years of life by 2040," says Gwen Nichols, M.D., Chief Medical Officer of LLS. "Advances in treatment and care, spearheaded by Dare to Dream, will give even more children a chance to grow and thrive into adulthood." People can donate to LLS at any time. From May 12-16, all donations made to LLS will go directly to The Dare to Dream Project. Interested in donating to The Dare to Dream Project? Visit this link for more information. About The Leukemia & Lymphoma Society The Leukemia & Lymphoma Society® (LLS) is the global leader in the fight against blood cancer. The LLS mission: Cure blood cancer and improve the quality of life of all patients and their families. LLS funds lifesaving blood cancer research around the world, provides free information and support services, and is the voice for all blood cancer patients seeking access to quality, affordable, coordinated care. Founded in 1949, LLS has regions throughout the United States and Canada. To learn more, visit . Patients should contact the Information Resource Center at (800) 955-4572, Monday through Friday, 9 a.m. to 9 p.m. ET. For additional information, visit lls.org/lls-newsnetwork. Follow us on Facebook, X, Instagram, LinkedIn and TikTok. About The Dare to Dream Project Dare to Dream exists to transform treatment and care for kids with blood cancer. Because kids are different and need to be treated differently, Dare to Dream funds groundbreaking research and the LLS PedAL Master Clinical Trial as well as expands LLS support services and drives advocacy efforts to help all kids with blood cancers get accessible, affordable, quality healthcare. LLS proudly and gratefully acknowledges all those contributing to the LLS mission, including corporate partners Walgreens, Valvoline™ Global Operations, The Wawa Foundation, and Subaru of America, Inc. and its retailers who have each pledged over $1 million to Dare to Dream. LLS also recognizes Sarah Asma and the Moore family; The Don & Lorraine Freeberg Foundation; The Harry T. Mangurian Jr. Foundation; Norcross Foundation, Inc.; Joan and Paul Rubschlager; and The Bobby Zahurak Pediatric AML Research and Patient Support Fund for their outstanding contributions to Dare to Dream. For more information about Dare to Dream, including resources for patients and their families, trial details, and eligibility, visit: lls.org/dare-to-dream. About LLS PedAL As part of LLS's Dare to Dream Project, the Pediatric Acute Leukemia Master Trial (PedAL) is the first-of-its-kind global master clinical trial for pediatric acute leukemia patients that will fundamentally change how children are treated. Prior to enrolling in therapeutic trials, patients enroll in the PedAL Screening Trial (NCT04726241) to identify the unique tumor biology of each child's cancer and help them to match with the most promising treatment. The Screening Trial is currently open at multiple sites in the United States, Canada, Australia, and New Zealand. At this time, two PedAL therapeutic trials are open and actively enrolling patients in the U.S., Canada, Australia, New Zealand, Japan, and Europe, with more therapeutic trials planned for global execution. To learn more about PedAL, visit lls.org/dare-to-dream. PedAL would not be possible without the support of major foundation donors such as Gateway for Cancer Research, which pledged $1.5 million over three years to support genomic sequencing and flow cytometry, which is being conducted through the PedAL screening trial, and the Lisa Dean Moseley Foundation, which has committed $1.25 million over five years to support the PedAL Principal Investigators Fellowship Program, whose members are leading the PedAL screening trial and therapeutic trials. Media Contact: Sandra Salviejo Senior Director, Communications [email protected] Reference: 1 Juul-Dam KL et al. European Journal of Medical Genetics 2023 SOURCE The Leukemia & Lymphoma Society (LLS) WANT YOUR COMPANY'S NEWS FEATURED ON PRNEWSWIRE.COM? 440k+ Newsrooms & Influencers 9k+ Digital Media Outlets 270k+ Journalists Opted In GET STARTED