新闻
First patient dosed in a proof-of-concept study of Yaqrit’s advanced microbiome therapeutic YAQ001 in patients with Primary Sclerosing Cholangitis and Inflammatory Bowel Disease
临床研究
引进/卖出
上市批准引进/卖出
上市批准并购
免疫疗法引进/卖出细胞疗法
并购
抗体药物偶联物
并购高管变更
Ultragenyx Announces First Patient Dosed in Aurora Study Evaluating GTX-102 in Additional Angelman Syndrome Genotypes and Age Groups
孤儿药快速通道突破性疗法寡核苷酸